Günther, RenéRenéGüntherWurster, Claudia DianaClaudia DianaWursterBrakemeier, SvenjaSvenjaBrakemeierOsmanovic, AlmaAlmaOsmanovicSchreiber-Katz, OliviaOliviaSchreiber-KatzPetri, SusanneSusannePetriUzelac, ZeljkoZeljkoUzelacHiebeler, MiriamMiriamHiebelerThiele, SimoneSimoneThieleWalter, Maggie C.Maggie C.WalterHagenacker, TimTimHagenacker2024-03-042024-03-042024https://resolver.sub.uni-goettingen.de/purl?gro-2/142198enhttps://www.elsevier.com/tdm/userlicense/1.0/Long-term efficacy and safety of nusinersen in adults with 5q spinal muscular atrophy: a prospective European multinational observational studyjournal_article10.1016/j.lanepe.2024.100862S2666776224000280