Prukop, ThomasThomasPrukopWernick, StephanieStephanieWernickBoussicault, LydieLydieBoussicaultEwers, DavidDavidEwersJäger, KarolineKarolineJägerAdam, JuliaJuliaAdamWinter, LorenzLorenzWinterQuintes, SusanneSusanneQuintesLinhoff, LisaLisaLinhoffBarrantes‐Freer, AlonsoAlonsoBarrantes‐FreerBartl, MichaelMichaelBartlCzesnik, DirkDirkCzesnikZschüntzsch, JanaJanaZschüntzschSchmidt, JensJensSchmidtPrimas, GwenaëlGwenaëlPrimasLaffaire, JulienJulienLaffaireRinaudo, PhilippePhilippeRinaudoBrureau, AnthonyAnthonyBrureauNabirotchkin, SergueiSergueiNabirotchkinSchwab, Markus H.Markus H.SchwabNave, Klaus‐ArminKlaus‐ArminNaveHajj, RodolpheRodolpheHajjCohen, DanielDanielCohenSereda, Michael W.Michael W.Sereda2021-04-142021-04-142020https://resolver.sub.uni-goettingen.de/purl?gro-2/81010enSynergistic PXT3003 therapy uncouples neuromuscular function from dysmyelination in male Charcot–Marie–Tooth disease type 1A (CMT1A) ratsjournal_article10.1002/jnr.24679